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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Modificateurs de gènes
Muscle development
Duchenne DMD dystrophy
Antisense oligonucleotides
CD38
Energy Metabolism/drug effects
Duchenne muscular dystrophy
DMD
Gene modifiers
Duchenne muscular dystrophy DMD
LncARN
Inbred C57BL
Molecular Sequence Data
Morphogenesis
Mice
BMD
CaV subunits
Humans
Muscle Biology
Myotendinous junction
Becker muscular dystrophy
Dystrophie Musculaire de Duchenne DMD
Cell Biology
Hepatocellular carcinoma
Ex-vivo
Myogenesis
Long QT
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Muscle Strength
Dystrophie Musculaire de Becker BMD
Delivery
Skeletal muscle
Epigenetics
Drp1
Mdx mouse
Cultured
Genomic
Cell Line
Gene Expression Regulation/drug effects
Knockout
Génomique
Inbred mdx
Becker BMD muscular dystrophy
CTNNB1
Invivo
Muscular dystrophy
DHPR α1S
Male
Base Sequence
Muscular Dystrophy
Dystrophin
Dynamin 2
LncRNA
Human Umbilical Vein Endothelial Cells
LKB1
Hear
NAD+
Animals
Cardiomyopathie
Multiresolution modeling
Dystrophine
Mitochondrial fission
Calcium Channels
Becker muscular dystrophy BMD
Long noncoding RNA
Metabolism
Cardiomyopathy
Centronuclear myopathy
Molecular docking
Liver
Clinical trials
Gene expression
Dystrophin central domain
Animal/physiopathology
Muscular Atrophy
Multi resolution modeling
NNOS
Inhibitors
CaVβs
Exon skipping
Muscles/physiopathology
MES
Muscle
Diseases
Cells
Cachexia
Calcium
MiARN
Immunoglobulin Fc Fragments/pharmacology
Dystrophin-EGFP
DMO
Allele‐specific silencing therapy
L-Type
Activin Receptors
Autophagy
Multi exon skipping
Dystrophy
Cell homeostasis
Homeostasis
Dystrophie musculaire de Becker